Opendata, web and dolomites
H2020 projects about "gangliosidosis"
The page lists 2 projects related to the topic "gangliosidosis".
| # | |||
|---|---|---|---|
| 1 | Sphingolead | Development of a potent dual GCS/GBA2 inhibitor as a best in class Gaucher therapeutic | 2016 |
| 2 | GT-GM1 | Ex vivo gene therapy for GM1-gangliosidosis | 2020 |