Opendata, web and dolomites

H2020 projects about "aav"

The page lists 16 projects related to the topic "aav".

# achronym  title  year 
1 GLYCODIS3 Genetic correction of glycogen debranching enzyme deficiency in Glycogen Storage disease III: a proof of concept study 2016
2 MINERVA Micro-RNAs of neutrophils in renal ANCA-associated vasculitis 2016
3 REGENETHER Modeling and treating retinal degenerative disease 2015
4 MYOCURE Development of an innovative gene therapy platform to cure rare hereditary muscle disorders 2016
5 EYEGET Gene therapy of inherited retinal diseases 2017
6 GeneVision Developing a cure for retinitis pigmentosa due to Usher syndrome 2017
7 VDJtargeting Engineering T cells and B cells for Immunotherapy using V(D)J recombination 2017
8 UshTher Clinical trial of gene therapy with dual AAV vectors for retinitis pigmentosa in patients with Usher syndrome type IB 2018
9 CureCN Adeno-Associated Virus Vector-Mediated Liver Gene Therapy for Crigler-Najjar Syndrome 2018
10 DIAMONDCOR A molecular approach to treat diabetes mellitus onset dependent coronaropathy 2018
11 MITOPOMPE Targeting mitochondrial defects and oxidative stress in Pompe Disease: from pathogenesis to therapy 2019
12 NEVULA Understanding selective neuronal vulnerability in Alzheimer’s disease 2018
13 CG01 A novel gene therapy for epilepsy 2018
14 CuRE Cardiac REgeneration from within 2019
15 iHEAR Gene therapy of inherited and acquired hearing loss 2019
16 inSight Moving a novel gene therapy paradigm to treat blindness to the market 2019