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MIN4ALD SIGNED

Use of MIN-102 for the treatment of children with cerebral ALD

Total Cost €

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EC-Contrib. €

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Partnership

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 MIN4ALD project word cloud

Explore the words cloud of the MIN4ALD project. It provides you a very rough idea of what is the project "MIN4ALD" about.

treatment    indicated    cald    cerebral    death    rare    amount    phenotype    orphan    aggressive    demonstrated    diseases    suppose    business    devastating    holds    feasibility    excellent    cognitive    disorder    pharmaceutical    cell    minoryx    stimulus    huge    usually    hematopoietic    motor    received    internationally    patients    always    alternative    linked    transplantation    nerve    stem    boy    pharma    time    cells    expand    leaders    24    visual    childhood    2022    procedure    niche    consolidation    min    valued    global    optimal       brain    central    pharmacological    fda    opportunity    reference    fatal    raised       drug    candidate    period    nervous    disease    market    576    cagr    us    itself    paediatric    102    adrenoleukodystrophy    therapy    2015    patent    121    occurring    min4ald    billion    genetic    opinion    auditory    demonstration    investors    onset    impressive    ald    designation    symptoms    company    progressive    function    grow    treat   

Project "MIN4ALD" data sheet

The following table provides information about the project.

Coordinator
MINORYX THERAPEUTICS S.L. 

Organization address
address: AVENIDA ERNEST LLUCH 32, TCM3, TECNOCAMPUS MATARO
city: MATARO BARCELONA
postcode: 8302
website: n.a.

contact info
title: n.a.
name: n.a.
surname: n.a.
function: n.a.
email: n.a.
telephone: n.a.
fax: n.a.

 Coordinator Country Spain [ES]
 Total cost 4˙437˙500 €
 EC max contribution 3˙106˙250 € (70%)
 Programme 1. H2020-EU.3. (PRIORITY 'Societal challenges)
2. H2020-EU.2.3. (INDUSTRIAL LEADERSHIP - Innovation In SMEs)
3. H2020-EU.2.1. (INDUSTRIAL LEADERSHIP - Leadership in enabling and industrial technologies)
 Code Call H2020-SMEInst-2018-2020-2
 Funding Scheme SME-2
 Starting year 2018
 Duration (year-month-day) from 2018-10-01   to  2021-03-31

 Partnership

Take a look of project's partnership.

# participants  country  role  EC contrib. [€] 
1    MINORYX THERAPEUTICS S.L. ES (MATARO BARCELONA) coordinator 3˙106˙250.00

Map

 Project objective

The objective of the MIN4ALD project is the development of a new pharmacological therapy to treat paediatric patients with cerebral ALD (cALD) - the most rapidly progressive and devastating phenotype of X-ALD (X-linked adrenoleukodystrophy).

cALD is a rare, fatal genetic disorder that affects nerve cells in the brain. Symptoms of cALD usually occur in a boy’s early childhood, and are characterized by rapidly progressive loss of visual, auditory, motor and cognitive function, with death usually occurring after 2 to 4 years from disease onset.

Currently, there is no pharmacological treatment available on the market. The only existing alternative for cALD patients is hematopoietic stem cell transplantation, yet the procedure itself is very aggressive and results are not always optimal.

Minoryx has developed a candidate drug that has demonstrated in several studies an excellent potential to treat patients with X-ALD. MIN4ALD Phase 2 demonstration is key to bring this unique treatment to the market. The results obtained in the Feasibility Analysis carried out indicated that MIN4ALD could be a huge business opportunity within the orphan diseases market.

The Global orphan diseases market is a niche market valued at US$ 121.6 billion in 2015. It is expected to grow to US$ 576.9 billion by 2022, with an average CAGR of 24.9% during the period 2015-2022. This is an impressive growth compared to the Global pharma market, which projects a 6.3% CAGR through 2022.

Minoryx has raised an important funding amount for R&D development from leading investors and has the support of reference Key Opinion Leaders. Minoryx received Orphan Drug Designation from both EU and FDA and holds a patent application covering the use of MIN-102 for X-ALD and other diseases affecting the central nervous system.

MIN4ALD will suppose a crucial stimulus for Minoryx to expand internationally and improve time-to-market, leading to the consolidation of the company in the pharmaceutical market.

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The information about "MIN4ALD" are provided by the European Opendata Portal: CORDIS opendata.

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