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H2020 projects about "orphan"

The page lists 60 projects related to the topic "orphan".

# achronym  title  year 
1 DE-ORPHAN DEtermination of Orphan Receptor PHysiological Agonists and sigNals 2015
2 RETHRIM Restoring tissue regeneration in patients with visceral Graft versus Host Disease. 2015
3 SC0806 Regenerative treatment of complete Traumatic Spinal Cord injury with a surgical implantation of a biodegradable device with FGF1 and nerve grafts 2015
4 ROR2BONE Investigating Ror2-dependent non-canonical Wnt signaling in bone remodeling 2015
5 FraxiFam Reconstructing gene family evolution in the ash genus (Fraxinus 2015
6 DEALS Biomarker assay development to expedite ALS experimental therapeutic advancement 2015
7 GLIOMARK Validation of blood-brain-barrier permeability as a glioma biomarker by means of the radiotracer 99mTc-tetrofosmin and single-photon emission computer tomography 2015
8 PRION2020 Function and malfunction of the prion protein 2015
9 TETRA Autologous Stem Cell Seeded Tissue Engineered Trachea 2016
10 FAST-DEVELOPS Developing new therapeutics for Friedreich ataxia 2015
11 SCIDNET DevelopIng Genetic medicines for Severe Combined Immunodeficiency (SCID) 2016
12 VISION DMD VISION-DMD - Phase 2 Clinical Trials of VBP15: An Innovative Steroid-like Intervention on Duchenne Muscular Dystrophy 2016
13 MYOCURE Development of an innovative gene therapy platform to cure rare hereditary muscle disorders 2016
14 H2020MM04 DC-based immunotherapy to treat Malignant Mesothelioma 2016
15 AML-VACCiN Clinical development of a dendritic-cell vaccine therapy for acute myeloid leukaemia 2016
16 WISLAS Warmed Icelandic Soils, Lipids and Sequencing: towards a better understood climate proxy 2016
17 RiboDisc Discovery of novel orphan riboswitch ligands 2016
18 BCM-UPS Dissecting the role of the ubiquitin proteasome system in the pathogenesis and therapy of B-cell malignancies 2016
19 EMODI Epithelial resistance modulation to treat disease 2016
20 NOTID Novel treatment of inflammatory diseases 2016
21 OVOMATIC IN-OVO AUTOMATION FOR CANCER DRUG DISCOVERY 2017
22 CureTheCloves PIK3CA inhibition in patients with the CLOVES syndrome 2017
23 CoALIVE Coenzyme A – Launch of In Vivo Experiments 2017
24 GeneVision Developing a cure for retinitis pigmentosa due to Usher syndrome 2017
25 Genome Biologics Reducing the cost and increasing the speed of preclinical research in the pharmaceutical industry 2017
26 CISTEM Heart On chip based on induced pluripotent Stem cell Technology for personalized Medicine 2018
27 TERRESTREVOL Exploring terra incognita: terrestrialization of arthropods in the era of genomics 2018
28 UshTher Clinical trial of gene therapy with dual AAV vectors for retinitis pigmentosa in patients with Usher syndrome type IB 2018
29 MCDS-Therapy Repurposing of carbamazepine for treatment of skeletal dysplasia 2017
30 RECOMB Stem-cell based gene therapy for recombination deficient SCID (RECOMB) 2018
31 CLINGLIO A Clinical Phase IIB trial with 2OHOA in patients with newly-diagnosed malignant glioma. 2017
32 OligoGpivotalCF A pivotal phase IIb clinical trial of inhaled alginate oligosaccharide (OligoG) for cystic fibrosis 2018
33 AirBorne AerIal RoBotic technologies for professiOnal seaRch aNd rescuE 2018
34 EDROMA Novel nanomedicine for the treatment of glioma 2018
35 CodingHeart Novel Coding Factors in Heart Disease 2019
36 CARAMBA SLAMF7-CAR T cells prepared by Sleeping Beauty gene-transfer for immunotherapy of multiple myeloma – a rare hematologic disease 2018
37 SMARTRIOX Disruptive targeted drug delivery system via synergistic combination of intelligent DNA molecular machines and gated mesoporous nanoparticles 2018
38 PAH-HOPE New hope for the PAH patient: A Novel Therapeutic for Pulmonary Arterial Hypertension (PAH) 2018
39 GENBIO Reducing the cost, time, and ethical burden of preclinical research in the pharmaceutical industry 2018
40 KHON2bTREAT Late Clinical Development of KH176: an innovative orphan drug to reach mitochondrial disease patients & market 2018
41 MIN4ALD Use of MIN-102 for the treatment of children with cerebral ALD 2018
42 denovoSkin Personalized, bio-engineered skin grafts for the permanent treatment of skin defects. 2018
43 NeuroProtect Novel Drug Therapy with Potential to Cure Neuro-Degenerative Diseases 2018
44 denovoSkin Personalized, bio-engineered skin grafts for the permanent treatment of skin defects 2018
45 Treat-HSP Development of new therapy for rare motor neuron diseases 2018
46 BERMES A Novel BERberine derivative for Malignant MESothelioma 2018
47 iProg Tailored cell-based therapies for frontotemporal dementia and related genetically defined CNS orphan indications 2018
48 TOL2 An effective and safe targeted therapy for treatment of Myasthenia gravis 2018
49 deCrYPtion Decrypting Mycobacterium cytochrome P450 (CYP) physiological functions by testing hypotheses emitted form large-scale comparative genomics analysis 2019
50 SUPERTEFF A new paradigm in boosting orphan crops to super grains: Linking metabolomics and gene editing to improve Teff for global food security and sustainable agriculture 2020
51 Hyalcis Hyaluronic-Cisplatin Film for Implant in Malignant Mesothelioma Recurrence 2019
52 RAPID The first effective remedy for acute pancreatitis disease 2019
53 Chelator IRON CHELATOR NBMI FOR THE TREATMENT OF IRON OVERLOAD IN BETA-THALASSEMIA MAJOR 2019
54 SPELITEC Sequence sPecific ELImination of shiga-Toxin E. Coli 2019
55 3TR Identification of the Molecular Mechanisms of non-response to Treatments, Relapses and Remission in Autoimmune, Inflammatory, and Allergic Conditions 2019
56 TRS A paradigm change in the treatment of blinding ocular diseases 2019
57 MaxONCO A cancer vaccine to boost body’s natural defences to fight chordoma and head and neck cancer 2020
58 NeuroPa Targeting the brain sigma-1 receptor: A paradigm shift for the treatment of neuro-degenerative disorders 2019
59 RD-MRI NETWORK BRIDGING THE GAP BETWEEN ACADEMIA & CLINICAL TRIALS FOR THE DEVELOPMENT OF RARE DISEASE TREATMENTS VIA NUCLEAR MAGNETIC RESONANCE IMAGING (MRI) 2020
60 ERA Epigenetic Regulation in Acinetobacter baumannii 2020